Статті в журналах з теми "CRISPR, Gene editing, Parkinson, Gene therapy"
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Ознайомтеся з топ-50 статей у журналах для дослідження на тему "CRISPR, Gene editing, Parkinson, Gene therapy".
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Chung, Sun-Ku, and Seo-Young Lee. "Advances in Gene Therapy Techniques to Treat LRRK2 Gene Mutation." Biomolecules 12, no. 12 (December 5, 2022): 1814. http://dx.doi.org/10.3390/biom12121814.
Повний текст джерелаRahman, Mujeeb ur, Muhammad Bilal, Junaid Ali Shah, Ajeet Kaushik, Pierre-Louis Teissedre, and Małgorzata Kujawska. "CRISPR-Cas9-Based Technology and Its Relevance to Gene Editing in Parkinson’s Disease." Pharmaceutics 14, no. 6 (June 13, 2022): 1252. http://dx.doi.org/10.3390/pharmaceutics14061252.
Повний текст джерелаDe Plano, Laura M., Giovanna Calabrese, Sabrina Conoci, Salvatore P. P. Guglielmino, Salvatore Oddo, and Antonella Caccamo. "Applications of CRISPR-Cas9 in Alzheimer’s Disease and Related Disorders." International Journal of Molecular Sciences 23, no. 15 (August 5, 2022): 8714. http://dx.doi.org/10.3390/ijms23158714.
Повний текст джерелаKatzmann, Julius L., Arjen J. Cupido, and Ulrich Laufs. "Gene Therapy Targeting PCSK9." Metabolites 12, no. 1 (January 12, 2022): 70. http://dx.doi.org/10.3390/metabo12010070.
Повний текст джерелаTang, Xuanting. "CRISPR/Cas9-based genome engineering in HIV gene therapy." E3S Web of Conferences 233 (2021): 02004. http://dx.doi.org/10.1051/e3sconf/202123302004.
Повний текст джерелаS., Manasa M. "CRISPR-Cas9 gene editing technology in human gene therapy: the new realm of medicine." International Journal of Advances in Medicine 9, no. 4 (March 24, 2022): 513. http://dx.doi.org/10.18203/2349-3933.ijam20220796.
Повний текст джерелаPreece, Roland, and Christos Georgiadis. "Emerging CRISPR/Cas9 applications for T-cell gene editing." Emerging Topics in Life Sciences 3, no. 3 (April 2, 2019): 261–75. http://dx.doi.org/10.1042/etls20180144.
Повний текст джерелаLiu, Wenlou, Chunsheng Yang, Yanqun Liu, and Guan Jiang. "CRISPR/Cas9 System and its Research Progress in Gene Therapy." Anti-Cancer Agents in Medicinal Chemistry 19, no. 16 (January 23, 2020): 1912–19. http://dx.doi.org/10.2174/1871520619666191014103711.
Повний текст джерелаSalsman, Jayme, and Graham Dellaire. "Precision genome editing in the CRISPR era." Biochemistry and Cell Biology 95, no. 2 (April 2017): 187–201. http://dx.doi.org/10.1139/bcb-2016-0137.
Повний текст джерелаKanu, Gayathri A., Javad B. M. Parambath, Raed O. Abu Odeh, and Ahmed A. Mohamed. "Gold Nanoparticle-Mediated Gene Therapy." Cancers 14, no. 21 (October 31, 2022): 5366. http://dx.doi.org/10.3390/cancers14215366.
Повний текст джерелаKhan, Sikandar Hayat. "Type-2 Diabetes and Gene Therapy: The Promise of CRISPR Gene Therapy in type-2 Diabetes Mellitus." Journal Of Obesity Management 1, no. 3 (September 23, 2019): 1–5. http://dx.doi.org/10.14302/issn.2574-450x.jom-19-3001.
Повний текст джерелаNaso, Gaetano, and Anastasia Petrova. "CRISPR/Cas9 gene editing for genodermatoses: progress and perspectives." Emerging Topics in Life Sciences 3, no. 3 (April 5, 2019): 313–26. http://dx.doi.org/10.1042/etls20180148.
Повний текст джерелаKoniali, Lola, Carsten W. Lederer, and Marina Kleanthous. "Therapy Development by Genome Editing of Hematopoietic Stem Cells." Cells 10, no. 6 (June 14, 2021): 1492. http://dx.doi.org/10.3390/cells10061492.
Повний текст джерелаBonillo, Mario, Julia Pfromm, and M. Dominik Fischer. "Challenges to Gene Editing Approaches in the Retina." Klinische Monatsblätter für Augenheilkunde 239, no. 03 (March 2022): 275–83. http://dx.doi.org/10.1055/a-1757-9810.
Повний текст джерелаRosenblum, Daniel, Anna Gutkin, Ranit Kedmi, Srinivas Ramishetti, Nuphar Veiga, Ashley M. Jacobi, Mollie S. Schubert, et al. "CRISPR-Cas9 genome editing using targeted lipid nanoparticles for cancer therapy." Science Advances 6, no. 47 (November 2020): eabc9450. http://dx.doi.org/10.1126/sciadv.abc9450.
Повний текст джерелаGarcía-Fernández, Alba, Gema Vivo-Llorca, Mónica Sancho, Alicia Belén García-Jareño, Laura Ramírez-Jiménez, Eloísa Barber-Cano, José Ramón Murguía, Mar Orzáez, Félix Sancenón, and Ramón Martínez-Máñez. "Nanodevices for the Efficient Codelivery of CRISPR-Cas9 Editing Machinery and an Entrapped Cargo: A Proposal for Dual Anti-Inflammatory Therapy." Pharmaceutics 14, no. 7 (July 19, 2022): 1495. http://dx.doi.org/10.3390/pharmaceutics14071495.
Повний текст джерелаFang, Ton, Goun Je, Peter Pacut, Kiandokht Keyhanian, Jeff Gao, and Mehdi Ghasemi. "Gene Therapy in Amyotrophic Lateral Sclerosis." Cells 11, no. 13 (June 29, 2022): 2066. http://dx.doi.org/10.3390/cells11132066.
Повний текст джерелаRen, Duohao, Sylvain Fisson, Deniz Dalkara, and Divya Ail. "Immune Responses to Gene Editing by Viral and Non-Viral Delivery Vectors Used in Retinal Gene Therapy." Pharmaceutics 14, no. 9 (September 19, 2022): 1973. http://dx.doi.org/10.3390/pharmaceutics14091973.
Повний текст джерелаPsatha, Nikoletta, Kiriaki Paschoudi, Anastasia Papadopoulou, and Evangelia Yannaki. "In Vivo Hematopoietic Stem Cell Genome Editing: Perspectives and Limitations." Genes 13, no. 12 (November 27, 2022): 2222. http://dx.doi.org/10.3390/genes13122222.
Повний текст джерелаKesavan, Gokul. "Emerging Gene Editing Therapies for Blood Disorders." Biotechnology Kiosk 3, no. 7 (July 30, 2021): 3–16. http://dx.doi.org/10.37756/bk.21.3.7.1.
Повний текст джерелаSun, Jinyu, Jianchu Wang, Donghui Zheng, and Xiaorong Hu. "Advances in therapeutic application of CRISPR-Cas9." Briefings in Functional Genomics 19, no. 3 (November 26, 2019): 164–74. http://dx.doi.org/10.1093/bfgp/elz031.
Повний текст джерелаZhao, Lan, Jian Huang, Yunshan Fan, Jun Li, Tianming You, Shisheng He, Guozhi Xiao, and Di Chen. "Exploration of CRISPR/Cas9-based gene editing as therapy for osteoarthritis." Annals of the Rheumatic Diseases 78, no. 5 (March 6, 2019): 676–82. http://dx.doi.org/10.1136/annrheumdis-2018-214724.
Повний текст джерелаKochergin-Nikitsky, K. S., E. V. Zaklyazminskaya, A. V. Lavrov, and S. A. Smirnikhina. "Cardiomyopathies associated with the DES gene mutations: molecular pathogenesis and gene therapy approaches." Almanac of Clinical Medicine 47, no. 7 (December 22, 2019): 603–13. http://dx.doi.org/10.18786/2072-0505-2019-47-025.
Повний текст джерелаMeiliana, Anna, Nurrani Mustika Dewi, and Andi Wijaya. "Genome Editing with Crispr-Cas9 Systems: Basic Research and Clinical Applications." Indonesian Biomedical Journal 9, no. 1 (April 1, 2017): 1. http://dx.doi.org/10.18585/inabj.v9i1.272.
Повний текст джерелаTeng, Man, Yongxiu Yao, Venugopal Nair, and Jun Luo. "Latest Advances of Virology Research Using CRISPR/Cas9-Based Gene-Editing Technology and Its Application to Vaccine Development." Viruses 13, no. 5 (April 28, 2021): 779. http://dx.doi.org/10.3390/v13050779.
Повний текст джерелаShaikh, Sadiya Bi, and Yashodhar Prabhakar Bhandary. "CRISPR/Cas9 Genome Editing Tool: A Promising Tool for Therapeutic Applications on Respiratory Diseases." Current Gene Therapy 20, no. 5 (December 11, 2020): 333–46. http://dx.doi.org/10.2174/1566523220666201012145731.
Повний текст джерелаGamage, Udani, Kesari Warnakulasuriya, Sonali Hansika та Gayathri N. Silva. "CRISPR Gene Therapy: A Promising One-Time Therapeutic Approach for Transfusion-Dependent β-Thalassemia—CRISPR-Cas9 Gene Editing for β-Thalassemia". Thalassemia Reports 13, № 1 (6 лютого 2023): 51–69. http://dx.doi.org/10.3390/thalassrep13010006.
Повний текст джерелаZhang, Zhihao, Wei Hou, and Shuliang Chen. "Updates on CRISPR-based gene editing in HIV-1/AIDS therapy." Virologica Sinica 37, no. 1 (February 2022): 1–10. http://dx.doi.org/10.1016/j.virs.2022.01.017.
Повний текст джерелаNakamura, Watanabe, Ando, Ishihara, and Sato. "Transplacental Gene Delivery (TPGD) as a Noninvasive Tool for Fetal Gene Manipulation in Mice." International Journal of Molecular Sciences 20, no. 23 (November 25, 2019): 5926. http://dx.doi.org/10.3390/ijms20235926.
Повний текст джерелаNie, Dengyun, Ting Guo, Miao Yue, Wenya Li, Xinyu Zong, Yinxing Zhu, Junxing Huang, and Mei Lin. "Research Progress on Nanoparticles-Based CRISPR/Cas9 System for Targeted Therapy of Tumors." Biomolecules 12, no. 9 (September 5, 2022): 1239. http://dx.doi.org/10.3390/biom12091239.
Повний текст джерелаYu, Jiaying, Xi Xiang, Jinrong Huang, Xue Liang, Xiaoguang Pan, Zhanying Dong, Trine Skov Petersen, et al. "Haplotyping by CRISPR-mediated DNA circularization (CRISPR-hapC) broadens allele-specific gene editing." Nucleic Acids Research 48, no. 5 (January 16, 2020): e25-e25. http://dx.doi.org/10.1093/nar/gkz1233.
Повний текст джерелаGodbout, Kelly, and Jacques P. Tremblay. "Prime Editing for Human Gene Therapy: Where Are We Now?" Cells 12, no. 4 (February 7, 2023): 536. http://dx.doi.org/10.3390/cells12040536.
Повний текст джерелаBalon, Katarzyna, Adam Sheriff, Joanna Jacków, and Łukasz Łaczmański. "Targeting Cancer with CRISPR/Cas9-Based Therapy." International Journal of Molecular Sciences 23, no. 1 (January 5, 2022): 573. http://dx.doi.org/10.3390/ijms23010573.
Повний текст джерелаLebek, Simon, Francesco Chemello, Xurde M. Caravia, Wei Tan, Hui Li, Kenian Chen, Lin Xu, Ning Liu, Rhonda Bassel-Duby та Eric N. Olson. "Ablation of CaMKIIδ oxidation by CRISPR-Cas9 base editing as a therapy for cardiac disease". Science 379, № 6628 (13 січня 2023): 179–85. http://dx.doi.org/10.1126/science.ade1105.
Повний текст джерелаBenati, Daniela, Amy Leung, Pedro Perdigao, Vasileios Toulis, Jacqueline van der Spuy, and Alessandra Recchia. "Induced Pluripotent Stem Cells and Genome-Editing Tools in Determining Gene Function and Therapy for Inherited Retinal Disorders." International Journal of Molecular Sciences 23, no. 23 (December 3, 2022): 15276. http://dx.doi.org/10.3390/ijms232315276.
Повний текст джерелаLyu, Pin, Luxi Wang, and Baisong Lu. "Virus-Like Particle Mediated CRISPR/Cas9 Delivery for Efficient and Safe Genome Editing." Life 10, no. 12 (December 21, 2020): 366. http://dx.doi.org/10.3390/life10120366.
Повний текст джерелаZhou, Jun, Zhuoying Ren, Jie Xu, Jifeng Zhang, and Y. Eugene Chen. "Gene editing therapy ready for cardiovascular diseases: opportunities, challenges, and perspectives." Medical Review 1, no. 1 (October 1, 2021): 6–9. http://dx.doi.org/10.1515/mr-2021-0010.
Повний текст джерелаSantos, Renato, and Olga Amaral. "Advances in Sphingolipidoses: CRISPR-Cas9 Editing as an Option for Modelling and Therapy." International Journal of Molecular Sciences 20, no. 23 (November 24, 2019): 5897. http://dx.doi.org/10.3390/ijms20235897.
Повний текст джерелаXiu, Kemao, Laura Saunders, Luan Wen, Jinxue Ruan, Ruonan Dong, Jun Song, Dongshan Yang, et al. "Delivery of CRISPR/Cas9 Plasmid DNA by Hyperbranched Polymeric Nanoparticles Enables Efficient Gene Editing." Cells 12, no. 1 (December 30, 2022): 156. http://dx.doi.org/10.3390/cells12010156.
Повний текст джерелаPadmaswari, Made Harumi, Shilpi Agrawal, Mary S. Jia, Allie Ivy, Daniel A. Maxenberger, Landon A. Burcham, and Christopher E. Nelson. "Delivery challenges for CRISPR—Cas9 genome editing for Duchenne muscular dystrophy." Biophysics Reviews 4, no. 1 (March 2023): 011307. http://dx.doi.org/10.1063/5.0131452.
Повний текст джерелаYan, Biying, and Yaxuan Liang. "New Therapeutics for Extracellular Vesicles: Delivering CRISPR for Cancer Treatment." International Journal of Molecular Sciences 23, no. 24 (December 12, 2022): 15758. http://dx.doi.org/10.3390/ijms232415758.
Повний текст джерелаRabaan, Ali A., Hajir AlSaihati, Rehab Bukhamsin, Muhammed A. Bakhrebah, Majed S. Nassar, Abdulmonem A. Alsaleh, Yousef N. Alhashem, et al. "Application of CRISPR/Cas9 Technology in Cancer Treatment: A Future Direction." Current Oncology 30, no. 2 (February 6, 2023): 1954–76. http://dx.doi.org/10.3390/curroncol30020152.
Повний текст джерелаHou, Yujuan, Guillermo Ureña-Bailén, Tahereh Mohammadian Gol, Paul Gerhard Gratz, Hans Peter Gratz, Alicia Roig-Merino, Justin S. Antony, et al. "Challenges in Gene Therapy for Somatic Reverted Mosaicism in X-Linked Combined Immunodeficiency by CRISPR/Cas9 and Prime Editing." Genes 13, no. 12 (December 13, 2022): 2348. http://dx.doi.org/10.3390/genes13122348.
Повний текст джерелаChen, Guofang, Tingyi Wei, Hui Yang, Guoling Li, and Haisen Li. "CRISPR-Based Therapeutic Gene Editing for Duchenne Muscular Dystrophy: Advances, Challenges and Perspectives." Cells 11, no. 19 (September 22, 2022): 2964. http://dx.doi.org/10.3390/cells11192964.
Повний текст джерелаBischoff, Nadja, Sandra Wimberger, Marcello Maresca, and Cord Brakebusch. "Improving Precise CRISPR Genome Editing by Small Molecules: Is there a Magic Potion?" Cells 9, no. 5 (May 25, 2020): 1318. http://dx.doi.org/10.3390/cells9051318.
Повний текст джерелаHuang, Yong, Meiqi Shang, Tingting Liu, and Kejian Wang. "High-throughput methods for genome editing: the more the better." Plant Physiology 188, no. 4 (February 3, 2022): 1731–45. http://dx.doi.org/10.1093/plphys/kiac017.
Повний текст джерелаHussein, Mouraya, Mariano A. Molina, Ben Berkhout, and Elena Herrera-Carrillo. "A CRISPR-Cas Cure for HIV/AIDS." International Journal of Molecular Sciences 24, no. 2 (January 13, 2023): 1563. http://dx.doi.org/10.3390/ijms24021563.
Повний текст джерелаOmichi, Ryotaro, Seiji B. Shibata, Cynthia C. Morton, and Richard J. H. Smith. "Gene therapy for hearing loss." Human Molecular Genetics 28, R1 (June 22, 2019): R65—R79. http://dx.doi.org/10.1093/hmg/ddz129.
Повний текст джерелаJiang, David J., Christine L. Xu, and Stephen H. Tsang. "Revolution in Gene Medicine Therapy and Genome Surgery." Genes 9, no. 12 (November 26, 2018): 575. http://dx.doi.org/10.3390/genes9120575.
Повний текст джерелаNasrallah, Ali, Eric Sulpice, Farah Kobaisi, Xavier Gidrol, and Walid Rachidi. "CRISPR-Cas9 Technology for the Creation of Biological Avatars Capable of Modeling and Treating Pathologies: From Discovery to the Latest Improvements." Cells 11, no. 22 (November 15, 2022): 3615. http://dx.doi.org/10.3390/cells11223615.
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